{"meta":{"id":"https:\/\/api.iclient.ifeng.com\/ipadtestdoc?aid=ucms_7xaMifhaDxd","type":"doc","o":"1","documentId":"ucms_7xaMifhaDxd"},"body":{"newStatus":"1","documentId":"ucms_7xaMifhaDxd","staticId":"ucms_7xaMifhaDxd","title":"基因治疗公司uniQure(QURE.US)宣布达成超20亿美元B型血友病产品对外授权协议","shareTitle":"基因治疗公司uniQure(QURE.US)宣布达成超20亿美元B型血友病产品对外授权协议","thumbnail":"http:\/\/d.ifengimg.com\/w150_h106_q100\/x0.ifengimg.com\/res\/2020\/11330DFF731FB15B7C35A10288A3D0B3994615A1_size2838_w1259_h943.png","source":"港股挖掘机","author":"","editorcode":"weMedia","editTime":"2020-06-25 09:24:17","updateTime":"2020\/06\/25 09:24:17","wapurl":"http:\/\/\/\/feng.ifeng.com\/c\/7xaMifhaDxd","introduction":"","wwwurl":"http:\/\/\/\/feng.ifeng.com\/c\/7xaMifhaDxd","commentsUrl":"ucms_7xaMifhaDxd","commentCount":0,"text":"
<\/p>
智通财经APP获悉,6月24日,基因治疗公司uniQure NV(QURE.US)宣布与CSL Behring签订了许可协议,为CSL Behring提供uniQure对B型血友病患者的基因治疗产品etranacogene dezaparvovec的全球独家权利。<\/p>
Etranacogene dezaparvovec由AAV5病毒载体组成,该载体带有一个基因盒,该盒带有受专利保护的Padua IX变体(FIX-Padua)。这项合作利用了CSL Behring在血液学领域的强大全球影响力和商业基础设施,从而加速了Etranacogene dezaparvovec对全球B型血友病患者的可及性。<\/p>
<\/p>
根据协议条款,uniQure将获得4.5亿美元的前期现金付款,并有资格根据监管和商业里程碑获得最高16亿美元的付款。uniQure也将有资格获得分层两位数的特许权使用费,最高可达合作产生的产品净销售额的20%。<\/p>
另外,uniQure将负责完成HOPE-B关键性研究,制造过程验证以及Etranagenegene dezaparvovec的制造供应,直到这些能力转移给CSL Behring。uniQure根据协议进行的临床开发和监管活动将由CSL Behring偿还。CSL Behring将负责法规提交和Etranagenegene dezaparvovec的商业化。<\/p>","img":[{"url":"http:\/\/d.ifengimg.com\/mw640_q100\/x0.ifengimg.com\/res\/2020\/11330DFF731FB15B7C35A10288A3D0B3994615A1_size2838_w1259_h943.png","size":{"width":"640","height":"479"}},{"url":"http:\/\/d.ifengimg.com\/mw640_q100\/x0.ifengimg.com\/res\/2020\/E42DCF29AAA73A05180B818035B0CEE1AD360E33_size44_w713_h395.jpeg","size":{"width":"640","height":"354"}}],"summary":"智通财经APP获悉,6月24日,基因治疗公司uniQureNV(QURE.US)宣布与CSLBehring签订了许可协议,为CSLBehring提供uniQur","sharesummary":"智通财经APP获悉,6月24日,基因治疗公司uniQureNV(QURE.US)宣布与CSLBehring签订了许可协议,为CSLBehring提供uniQur","commentType":"0","wemediaEAccountId":"8516","showclient":"0","shareurl":"https:\/\/ishare.ifeng.com\/c\/s\/v0027LibN6h3NnPw5Y98u54bsCcE6E-_nkWYBfX2N15UeRTo__","praise":"1","like_num":"1"}}